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⚡ Current Task Assignment
🧬 Genetic Analysis
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📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
The purpose of the study is to determine if triheptanoin is an effective tr...
Status
Completed
Location
Department of Genetics, Groupe Hospitalier Pitié-Salpêtrière
Start Date
2009-06
Trial ID
NCT00947960
Treatments Being Tested
The primary objective of the study was to evaluate the impact of UX007 on a...
Status
Completed
Location
Children's National Medical Center
Start Date
2014-02-06
Trial ID
NCT01886378
Treatments Being Tested
The aim of this study is to investigate the effect of 14 days of treatment ...
Status
Completed
Location
Copenhagen Neuromuscular Center
Start Date
2018-08-15
Trial ID
NCT03642860
Treatments Being Tested
The main goal of this study is to evaluate the effects of triheptanoin vers...
Status
Active Not Recruiting
Location
General University Hospital in Prague-GUH (Všeobecná fakultní nemocnice v Praze- VFN)
Start Date
2023-02-28
Trial ID
NCT05933200
Treatments Being Tested
Patients with dilated cardiomyopathy who present for indwelling right heart...
Status
Withdrawn
Location
University of Texas-Southwestern
Start Date
2013-02
Trial ID
NCT01787851
Treatments Being Tested
The causes of ALS are largely unknown. However, mitochondrial dysfunction, ...
Status
Completed
Location
Duke University
Start Date
2018-06-21
Trial ID
NCT03506425
Treatments Being Tested
The purpose of this project is to study the efficacy of an anaplerotic trea...
Status
Completed
Location
Brain and Spine Institute
Start Date
2013-05
Trial ID
NCT01882062
Treatments Being Tested
The primary objectives of the study are to evaluate the efficacy of UX007 c...
Status
Completed
Location
Children's Hospital Colorado - University of Colorado, Denver, School of Medicine
Start Date
2014-02-28
Trial ID
NCT01993186
This is a compassionate use study to allow patients already taking trihepta...
Status
No Longer Available
Location
University of Pittsburgh Division of Medical Genetics, Children's Hospital of Pittsburgh
Start Date
TBD
Trial ID
NCT01461304
Treatments Being Tested
The purpose of this project is to study the efficacy of triheptanoin oil in...
Status
Completed
Location
Groupe hospitalier Pitié Salpêtrière
Start Date
2015-03-25
Trial ID
NCT02408354
Treatments Being Tested